Yayınlanmış 1 Ocak 2019 | Sürüm v1
Dergi makalesi Açık

Abatacept as a Long-Term Targeted Therapy for LRBA Deficiency

  • 1. Marmara Univ, Sch Med, Div Pediat Allergy & Immunol, Istanbul, Turkey
  • 2. Uludag Univ, Div Pediat Allergy & Immunol, Fac Med, Bursa, Turkey
  • 3. Cukurova Univ, Fac Med, Div Pediat Allergy Immunol, Adana, Turkey
  • 4. Ege Univ, Fac Med, Div Pediat Allergy & Immunol, Izmir, Turkey
  • 5. Kocaeli Univ, Fac Med, Div Pediat Allergy & Immunol, Kocaeli, Turkey
  • 6. Ankara Childrens Hematol Oncol Training & Res Hos, Div Pediat Hematol, Ankara, Turkey
  • 7. Erciyes Univ, Fac Med, Div Pediat Immunol, Kayseri, Turkey
  • 8. Necmettin Erbakan Univ, Fac Med, Div Pediat Allergy & Immunol, Konya, Turkey
  • 9. Ondokuz Mayis Univ, Fac Med, Div Pediat Allergy & Immunol, Samsun, Turkey
  • 10. Sidra Med, Res Branch, Div Translat Med, Doha, Qatar
  • 11. Istanbul Univ, Istanbul Med Fac, Div Pediat Infect Dis, Istanbul, Turkey
  • 12. Saglik Bilimleri Univ, Zeynep Kamil Women & Children Hosp, Med Fac, Div Pediat Endocrinol Clin, Istanbul, Turkey

Açıklama

BACKGROUND: LPS-responsive beige-like anchor (LRBA) deficiency presents with susceptibility to infections, autoimmunity, and lymphoproliferation. The long-term efficacy of cytotoxic T-lymphocyte-associated antigen 4-immunoglobulin (abatacept) as targeted therapy for its immune dysregulatory features remains to be established.

Dosyalar

bib-741769d6-2301-4b0e-a282-141cdeaa3aa7.txt

Dosyalar (387 Bytes)

Ad Boyut Hepisini indir
md5:4b08dfe97f2bd8e483c1c279530bccb9
387 Bytes Ön İzleme İndir